DrKrista Vandenborne

DTA Edgewise Therapeutics GRASP

Longitudinal Assessment of Molecular and Imaging Biomarkers in LGMDR1

Disease Progression Models Intended to Inform the Design of Studies for LGMD

Career Advancement and Development in Rehabilitation Research (CADRRE)

Data Transfer and Use Agreement between Wave Life Science USA, Inc. and University of Florida Board of Trustees

EMBARK DUA - PHASE 1

MR Assessment of the effect of nNOS on Bioenergetics and Microvascular Function in Becker and Duchenne Muscular Dystrophy

Model-Informed Clinical Trial Design for Duchenne Muscular Dystrophy: Modeling Treatment Effects and Enhancing Simulation Tools

Early Cardiac Biomarkers of Inflammation and Remodeling in DMD

Addressing Shortcomings of AAV GeneTherapies for the Muscular Dystrophies

MRI/MRS Markers of Skeletal Muscle Disease Progression and Vascular Function in Non-Ambulatory Individuals with DMD

Data Transfer and Use Agreement between Dyne Therapeutics, Inc. and University of Florida Board of Trustees - iDMD

Fuller T32 renewal

Trial Readiness and Endpoint Assessment in LGMDR1 (TREATing-LGMDR1)

Givinostat Phase 3 Clinical Trial in non-ambulant DMD boys

A Phase 2 Randomized, Double-blind, Placebo-controlled Study to Evaluate the Effect of EDG-5506 on Safety, Biomarkers, Pharmacokinetics, and Functional Measures in Adults and Adolescents with Becker Muscular Dystrophy

Natural History Data in Support of Randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of givinostat in ambulant patients with Duchenne Muscular Dystrophy

A Phase 1/2 Dose-escalation Study to Evaluate the Safety of LION-101 in Adult Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)

Data Transfer and Use Agreement between the UF and NS Pharma

Protein Mapping Project

Avidity Biosciences Data Transfer and Use Agreement

A Phase 1/2 Open-label, Dose Escalation and Dose Expansion Study to Evaluate the Safety, Tolerability, Pharmacodynamics, and Pharmacokinetics of Intravenous RGX-202 Gene Therapy in Males with Duchenne Muscular Dystrophy (DMD)

Microdystrophin Gene Transfer Study in Adolescents and Children With DMD (IGNITE DMD)

A Phase 3, Multinational, Randomized, Double-Blind, Placebo-Controlled Systemic Gene Transfer Therapy Study to Evaluate the Safety and Efficacy ofSRP-9001 in Non-Ambulatory and Ambulatory Subjects With Duchenne Muscular Dystrophy

Defining Endpoints in Becker Muscular Dystrophy - GRASP