MsJulie Berthy
AST SCTST
MD-PEDIATRICS
GRANTS
- GRANTRegistry Study to Observe Long-Term Safety of Vamorolone (AGAMREE®) in Patients with Duchenne Muscular Dystrophy, Protocol # DMD-001Catalyst Pharmaceuticals24 Jul 2025 - 23 Jul 2030
- GRANTResearch ECHOUniversity of Florida20 Feb 2024 - 19 Feb 2029
- GRANTA Phase 2 Study to Evaluate the Effect of EDG-5506 on Safety, Pharmacokinetics, and Biomarkers in Children and Adolescents with Duchenne Muscular Dystrophy Previously Treated with Gene TherapyEdgewise Therapeutics14 Dec 2023 - 13 Dec 2028
- GRANTA 2-Part, Phase 2 Study to Evaluate the Effect of EDG-5506 on Safety, Pharmacokinetics and Biomarkers in Children with Duchenne Muscular Dystrophy, which includes a Randomized, Double-Blind, Placebo-Controlled Dose-Ranging Part A Followed by Part B, an Open-Label ExtensionEdgewise Therapeutics9 May 2023 - 8 May 2028
- GRANTA Randomized, Double-Blind, Placebo-Controlled, Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Ambulatory and Non-Ambulatory Participants with Spinal Muscular Atrophy with Open-Label Extension (RESILIENT)Biohaven Pharmaceuticals4 Oct 2022 - 2 Oct 2027
- GRANTLifeGlider - mobility device solution to falls and loss of ambulationUF Medical Guild22 Sep 2022 - 31 May 2025
- GRANTTask Order #8: Documentation and Development in support of Clinical Programs in Friedreich’s Ataxia*aavantibio25 Jan 2021 - 31 Dec 2022